Status
Study
Lead sponsor
Phase
Enrol
Sites in Australia
Start
Recruiting
Boehringer Ingelheim
Phase 3
35
North Adelaide
2026-07-21
Recruiting
AstraZeneca
Phase 1/2
152
North Adelaide
2026-06-03
Recruiting
Axonics, Inc.
Not applicable
75
North Adelaide, East Melbourne
2026-04-30
Recruiting
Novartis Pharmaceuticals
Phase 2
50
Brisbane, North Adelaide
2026-04-28
Recruiting
RAPT Therapeutics, Inc., a member of the GSK plc group of companies
Phase 2
100
Darlinghurst, Westmead, South Brisbane, North Adelaide, Clayton, Parkville, Nedlands, Perth
2025-10-22
Recruiting
Novartis Pharmaceuticals
Phase 2
140
Sydney, North Adelaide
2025-10-09
Active, closed
Azafaros B.V.
Phase 3
75
North Adelaide
2025-06-30
Recruiting
Azafaros B.V.
Phase 3
72
North Adelaide, Parkville
2025-06-30
Recruiting
Azafaros B.V.
Phase 3
147
North Adelaide, Parkville
2025-06-30
Recruiting
Children's Oncology Group
Phase 2
240
Hunter Regional Mail Centre, Randwick, Westmead, South Brisbane, North Adelaide, Parkville, Perth
2024-10-22
Active, closed
Sanofi
Phase 2
185
Chermside, South Brisbane, North Adelaide, Box Hill, Fitzroy, Frankston
2024-06-20
Recruiting
PTC Therapeutics
Phase 3
56
North Adelaide, Parkville
2024-03-04
Recruiting
Frontier Medicines Corporation
Phase 1/2
403
Macquarie Park, Southport, Kurralta Park, North Adelaide, Box Hill, Nedlands
2024-02-12
Active, closed
Otsuka Australia Pharmaceutical Pty Ltd
Phase 3
13
Newcastle, Benowa, Townsville, North Adelaide, Ballarat Central, Traralgon
2023-12-20
Active, closed
Teva Branded Pharmaceutical Products R&D LLC
Phase 3
2,772
Box Hill, Clayton, Melbourne, Midland, Nedlands, North Adelaide, Parkville, South Brisbane
2023-08-30
By invitation
Vertex Pharmaceuticals Incorporated
Phase 3
174
Nedlands, North Adelaide, Parkville, South Brisbane
2023-08-11
Recruiting
GlaxoSmithKline
Phase 3
138
South Brisbane, North Adelaide, Joondalup WA
2023-04-24
Active, closed
Murdoch Childrens Research Institute
Not applicable
441
Randwick, North Adelaide, Parkville, Nedlands
2023-03-22
Active, closed
Day One Biopharmaceuticals, Inc.
Phase 3
418
South Brisbane, Nedlands, North Adelaide, Parkville, Randwick, Westmead
2023-02-27
Active, closed
Aravax Pty Ltd
Phase 2
90
Randwick, Westmead, South Brisbane, North Adelaide, Parkville, Nedlands
2023-02-09
Active, closed
Regeneron Pharmaceuticals
Phase 3
1,564
Blacktown, Lismore, Liverpool, Wollstonecraft, Bedford Park, North Adelaide, Box Hill, Geelong
2023-01-16
Recruiting
University of Michigan
Not applicable
900
Brisbane, Douglas, Southport, North Adelaide, Clayton, Parkville, Nedlands
2022-08-05
Active, closed
Regeneron Pharmaceuticals
Phase 3
1,546
Southport, Townsville, North Adelaide, Hobart, Geelong, Melbourne
2022-07-14
Active, closed
Vertex Pharmaceuticals Incorporated
Phase 3
210
Nedlands, North Adelaide, Parkville, South Brisbane
2022-06-21
Active, closed
Pierre Fabre Medicament
Phase 3
815
Sydney, Wollstonecraft, Woolloongabba, North Adelaide, Box Hill, Heidelberg, Prahran, Nedlands
2022-05-02
Active, closed
AstraZeneca
Phase 3
1,035
Birtinya, Greenslopes, Kogarah, North Adelaide, Orange, Redcliffe, Wahroonga
2022-03-25
Active, closed
BeOne Medicines
Phase 3
799
Concord, Gosford, Kogarah, Orange, Port Macquarie, Westmead, Douglas, North Adelaide
2022-03-10
Recruiting
Central Adelaide Local Health Network Incorporated
Not applicable
44
Adelaide, North Adelaide
2021-11-20
Recruiting
Children's Oncology Group
Phase 2
160
Randwick, Westmead, South Brisbane, North Adelaide, Parkville, Perth
2021-07-13
Active, closed
Columbia University
Observational
122
Adelaide, Chatswood, East Melbourne, Maribyrnong, North Adelaide, Subiaco, Sydney
2021-05-06
Recruiting
Children's Oncology Group
Phase 2
256
Hunter Regional Mail Centre, Randwick, Westmead, South Brisbane, North Adelaide, Clayton, Parkville, Perth
2020-10-19
Active, closed
Sabine Mueller, MD, PhD
Phase 1
9
Sydney, Westmead, South Brisbane, North Adelaide, Parkville, Perth
2020-10-02
By invitation
Ultragenyx Pharmaceutical Inc
Phase 3
41
North Adelaide
2020-09-28
Active, closed
Amicus Therapeutics
Phase 3
21
North Adelaide
2020-02-13
Recruiting
Children's Oncology Group
Phase 3
5,951
Hunter Regional Mail Centre, Westmead, South Brisbane, North Adelaide, Saint Hobart, Clayton, Parkville, Perth
2019-10-31
Active, closed
Children's Oncology Group
Phase 2
94
Hunter Regional Mail Centre, Randwick, Westmead, South Brisbane, North Adelaide, Parkville, Perth
2019-07-08
Active, closed
National Cancer Institute (NCI)
Phase 3
6,720
Hunter Regional Mail Centre, Westmead, South Brisbane, North Adelaide, Clayton, Parkville, Perth
2019-07-03
Active, closed
Exelixis
Phase 3
855
Albury, Kogarah, North Ryde, Sydney, South Brisbane, Woolloongabba, Adelaide, North Adelaide
2019-06-25
Recruiting
Monash University
Phase 3
336
Camperdown, Newcastle, South Brisbane, Southport, North Adelaide, Clayton, Heidelberg, Parkville
2019-05-29
Active, closed
Children's Oncology Group
Phase 3
537
Hunter Regional Mail Centre, Randwick, Westmead, South Brisbane, North Adelaide, Parkville, Perth
2018-05-24
Active, closed
Children's Oncology Group
Phase 2
45
Hunter Regional Mail Centre, North Adelaide, Perth
2017-11-17
Recruiting
Ultragenyx Pharmaceutical Inc
Phase 2/3
36
North Adelaide
2016-04-25
Active, closed
Genetix Biotherapeutics Inc.
Observational
64
North Adelaide
2016-01-22
Active, closed
Bayer
Phase 1/2
154
Sydney, North Adelaide, Parkville
2015-12-16
Recruiting
Children's Oncology Group
Observational
75,000
Hunter Regional Mail Centre, Randwick, Westmead, South Brisbane, North Adelaide, Saint Hobart, Clayton, Parkville
2015-11-03
Active, closed
Children's Oncology Group
Phase 3
158
Hunter Regional Mail Centre, Randwick, Westmead, South Brisbane, North Adelaide, Parkville, Perth
2015-07-21
Active, closed
National Cancer Institute (NCI)
Phase 3
847
Hunter Regional Mail Centre, Westmead, South Brisbane, North Adelaide, Clayton, Parkville, Perth
2014-10-04
Active, closed
Children's Oncology Group
Phase 3
391
Hunter Regional Mail Centre, Randwick, Westmead, South Brisbane, North Adelaide, Perth
2014-08-08
Recruiting
Poitiers University Hospital
Observational
750
North Adelaide
2011-01