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Compound · clinical trials

Nizubaglustat clinical trials

Also listed in trial records as AZ-3102
Source: ClinicalTrials.gov, U.S. National Library of Medicine — the 4 trials in our India, USA and UK registers that name Nizubaglustat as an intervention. Synced 25 Sep 2026
4Current trials
2Recruiting now
1Lead sponsor
3Country registers
Maintained by Sreepriya Prasannan
MSc Digital Transformation of Life Sciences (Innopharma Education / Griffith College); MSc & BSc Botany HSE Spark Ignite 2026 โ€” Top 14 finalist
Compiled from ClinicalTrials.gov registry records ยท Last verified ยท Editorial standards
At a glance

Nizubaglustat is named as an intervention in 4 current clinical trials in our India, USA and UK registers. 2 are recruiting patients now. The most common phase is Phase 3. The lead sponsor is Azafaros B.V. The most-studied condition is Niemann-Pick Type C Disease.

Trials by status

  • Recruiting250%
  • Not yet open125%
  • Active, closed125%

Trials by phase

  • Phase 3375%
  • Phase 2125%
01

Clinical trials of Nizubaglustat

4 trials
StudyPhaseStatusLead sponsorRegisters
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis
NCT07054515 · ClinicalTrials.gov ↗ · Niemann-Pick Type C Disease, GM1 Gangliosidosis, GM2 Gangliosidosis
Phase 3 Recruiting Azafaros B.V. UK, USA, India
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC)
NCT07082725 · ClinicalTrials.gov ↗ · Niemann-Pick Type C Disease
Phase 3 Recruiting Azafaros B.V. UK, USA, India
Study to Evaluate the Efficacy and Safety of Nizubaglustat (AZ-3102) in Patients With Gaucher Disease Type 3 (GD3)
NCT07715084 · Gaucher Disease Type 3
Phase 2 Not yet open Azafaros B.V. India
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis
NCT07082543 · Gangliosidoses, GM2, Gangliosidosis, GM1
Phase 3 Active, closed Azafaros B.V. USA, India

Registers list studies that are recruiting, about to open, active but closed to enrolment, or enrolling by invitation. The UK and USA registers cover industry-sponsored studies only. Trial titles and statuses are copied from the registry as published.

02

Conditions studied with Nizubaglustat

6 conditions
Niemann-Pick Type C Disease2GM1 Gangliosidosis1GM2 Gangliosidosis1Gangliosidoses, GM21Gangliosidosis, GM11Gaucher Disease Type 31
03

Sponsors

lead sponsor per trial
Lead sponsorTrials
Azafaros B.V.4
04

By country register

RegisterTrialsRecruiting
Clinical trials in India42
Clinical trials in USA32
Clinical trials in UK22

A trial with sites in more than one country appears in each of those registers.

05

Questions about Nizubaglustat trials

How many clinical trials are testing Nizubaglustat?

4 current trials in our India, USA and UK registers name Nizubaglustat (also registered as AZ-3102) as a drug or biological intervention, as of the registry sync on 25 September 2026. Completed and withdrawn studies are not counted.

Are Nizubaglustat trials recruiting patients?

Yes. 2 of the 4 trials are recruiting: 2 with sites in India, 2 with sites in USA and 2 with sites in UK. Eligibility and site contacts are on each trial's record. Only the study team can confirm whether a patient is eligible.

Who sponsors Nizubaglustat clinical trials?

The lead sponsor is Azafaros B.V. The number in brackets is how many trials each organisation leads.

Where does this information come from?

Every trial, status, phase and sponsor on this page is copied from public ClinicalTrials.gov records by a daily sync. Nothing here describes how Nizubaglustat works or whether it is effective, and it is not medical advice.

How this page is built

Everything on this page is copied from public ClinicalTrials.gov registry records โ€” it is not written from memory, and nothing here describes how Nizubaglustat works or whether it is effective. Each trial links to its own record so you can check it yourself.

This page is built automatically: a daily sync job reads the registry records behind our country trial registers, collects every trial that lists Nizubaglustat (or a registered synonym) as a drug or biological intervention, and tabulates the registry fields directly. Placebos and generic comparators are excluded. There is no AI drafting and no per-compound editorial pass, and the page has not been clinically reviewed. The “last verified” date above is the timestamp of that sync, not a review date. Our general editorial approach is described in our editorial standards and corrections policy. The ClinicalTrials.gov data on this page was last retrieved on 25 Sep 2026.

Please verify before you rely on this. This page is general information for life-science and pharmaceutical professionals. It is not medical advice, and it has not been reviewed by a clinician โ€” our editorial team holds life-science qualifications, not clinical ones. It is not exhaustive and may not reflect the most recent label change. Always check the official prescribing information (US Prescribing Information or EU SmPC) and speak to your doctor or pharmacist before acting on anything here. Drugs in the same class are not automatically interchangeable, and approvals, brand names and indications differ between the US, the EU/Ireland (EMA/HPRA) and other regions. Spotted an error? Tell us โ€” we correct promptly and log it.