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Clinical Trials in Italy / NCT05755451
Recruiting Observational

Natural History of SMA

NCT05755451 · tracked via the Priya Life Science Italy tracker
Sponsor
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Phase
Observational
Started
2018-06-21
Last updated
2023-03-06

Condition(s) studied

Muscular Atrophy, Spinal

Study summary

This is an investigator initiated observational study with the aim to record several aspects of function, care and adverse events in a large cohort of SMA patients followed longitudinally by using a structured academic disease registry.

Eligibility

Sex
ALL
Min age
—
Max age
—
Healthy volunteers
No
Inclusion Criteria: all patients Exclusion Criteria: if enrolled in clinical trials

Primary outcome measure(s)

  • motor function — 15 years
    functional scales Hammersmith Functional motor scale, (minimum score 0, maximum score 74 indicating best performance

Trial sites (5)

FacilityCityRegionStatus
Istituto Gaslini Genova Italy Recruiting
Nemo Sud Messina Italy Recruiting
Centro Clinico nemo Milan Italy Recruiting
Ospedale Bambino gesu Rome Italy Recruiting
Policlinico gemelli Rome Italy Recruiting

More Fondazione Policlinico Universitario Agostino Gemelli IRCCS trials in Italy

The Management of Asymptomatic Carotid Stenosis Recruiting
Modular Neurological Examination for Early Risk Detection Active, not recruiting
Encorafenib + Cetuximab Beyond Progression in Combination With FOLFIRI in Patients With BRAF V600E Mutated Metastatic Colorectal Cancer Progressing on Encorafenib + Cetuximab. Recruiting
BRCA Mutation Carriers' Platform a Multicenter Study Recruiting
Superior Cervical Ganglion in Parkinson's Disease Recruiting

Other trials for the same condition

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK) Recruiting
A Study to Learn About the Safety of BIIB115 Injections and How BIIB115 is Processed in the Bodies of Healthy Adult Male Volunteers and of Pediatric Participants With Spinal Muscular Atrophy Who Previously Took Onasemnogene Abeparvovec Active, not recruiting
Official registry record

This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.

View NCT05755451 on ClinicalTrials.gov ↗ ← All trials in Italy