A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping
Condition(s) studied
Investigational drug(s) / intervention(s)
AOC 1044: AOC 1044 will be administered by intravenous (IV) infusion
Placebo: Placebo will be administered by intravenous (IV) infusion
Study summary
A Randomized, Double-blind, Placebo-controlled, Phase 3 Study to Evaluate the Efficacy and Safety of Intravenous AOC 1044 for the treatment of Duchenne Muscular Dystrophy (DMD) with Gene Mutations Amenable to Exon 44 Skipping
Eligibility
Primary outcome measure(s)
- Change from Baseline in Time to Rise (TTR) Velocity at Week 54 — Baseline, Week 54
Trial sites (17)
| Facility | City | Region | Status |
|---|---|---|---|
| UZ Leuven | Leuven | Belgium | Recruiting |
| Centre Hospitalier Régional de la Citadelle | Liège | Belgium | Recruiting |
| CHU de Nantes - Hotel-Dieu | Nantes | France | Recruiting |
| AP-HP Hospital Armand-Trousseau | Paris | France | Recruiting |
| Universitaetsklinikum Essen | Essen | Germany | Recruiting |
| Universitaetsklinikum Heidelberg | Heidelberg | Germany | Recruiting |
| Klinikum der Ludwig-Maximilians-Universitaet Muenchen | München | Germany | Recruiting |
| Istituto Giannina Gaslini | Genova | Italy | Recruiting |
| Fondazione Serena ETS - Centro Clinico NeMO Milano | Milan | Italy | Recruiting |
| IRCCS Ospedale San Raffaele | Milan | Italy | Recruiting |
| Fondazione Policlinico Universitario A. Gemelli IRCCS - Universitario Cattolica del Sacro Cuore | Roma | Italy | Recruiting |
| Academisch Ziekenhuis Leiden | Leiden | Netherlands | Recruiting |
| Hospital Sant Joan de Deu | Barcelona | Spain | Recruiting |
| Hospital Universitario La Paz | Madrid | Spain | Recruiting |
| Hospital Viamed Santa Angela De la Cruz - FutureMeds Spain | Seville | Spain | Recruiting |
| Royal Victoria Infirmary | Newcastle | United Kingdom | Recruiting |
| University of Oxford and Oxford University Hospitals NHS Foundation Trust | Oxford | United Kingdom | Recruiting |
More Avidity Biosciences, Inc. trials in Spain
Other trials for the same condition
This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.
View NCT07587242 on ClinicalTrials.gov ↗ ← All trials in Spain