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Active, not recruiting Phase 3

A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Pediatric Participants With Atypical Hemolytic Uremic Syndrome (aHUS)

NCT04958265 · tracked via the Priya Life Science France tracker
Phase
Phase 3
Started
2021-11-17
Last updated
2026-10-01

Condition(s) studied

Atypical Hemolytic Uremic Syndrome

Investigational drug(s) / intervention(s)

Crovalimab →

Crovalimab: Crovalimab will be administered at a dose of 1000 mg intravenously (IV) (for participants weighing =\> 40 to \<100 kg) or 1500 mg IV (for participants weighing \>=100 kg) on Week 1 Day 1. On Week 1 Day 2 and on Weeks 2, 3 and 4, crovalimab will be administered at a dose of 340 mg subcutaneously (SC). On Week 5 and Q4W thereafter, it will be administered at a dose of 680 mg SC (for participants weighing =\> 40 to \<100 kg) or 1020 mg SC (for participants weighing \>=100 kg). Enrollment of participants weighing \<40 kg will be staggered using two weight-based dose confirmation groups (Group 1 participants weighing \>=20 kg to \<40 kg, followed by Group 2 participants weighing \>=5 kg to \<20 kg). All participants will receive an initial IV loading dose, which will be followed by SC dosing at either Q2W or Q4W intervals (depending on body weight), until study completion.

Study summary

This study aims to evaluate the efficacy and safety of crovalimab in pediatric participants with aHUS.

Eligibility

Sex
ALL
Min age
28 Days
Max age
17 Years
Healthy volunteers
No
Inclusion Criteria: * Body weight \>= 5 kg at screening. * Vaccination against Neisseria meningitis serotypes A, C, W, and Y; vaccination against serotype B, according to national vaccination recommendations. * Vaccination against Haemophilus influenzae type B and Streptococcus pneumoniae, according to national vaccination recommendations. * For patients continuing to receive other therapies concomitantly with crovalimab (e.g., immunosuppressants, corticosteroids, mammalian target of rapamycin inhibitor (mTORi), or calcineurin inhibitors): stable dose for \>=28 days prior to screening and up to the first crovalimab administration. * For female participants of childbearing potential: an agreement to remain abstinent or use contraception. * Participants with a prior kidney transplant are eligible if they have a known history of complement-mediated aHUS prior to the kidney transplant. * Onset of initial TMA presentation within 28 days prior to the first dose of crovalimab (for Naive Cohort only). * Documented treatment with either eculizumab or ravulizumab (for Switch Cohort only). * Clinical evidence of response to a C5 inhibitor (for Switch Cohort only). * Poorly controlled TMA following treatment with another C5 inhibitor (for C5 SNP participants in the Pretreated Cohort only). * Known C5 polymorphism (for C5 SNP participants in the Pretreated Cohort only). Exclusion Criteria: * TMA associated with non-aHUS related renal disease. * Positive direct Coombs test. * Chronic dialysis within 90 days prior to first crovalimab administration , and /or end stage renal disease * Identified drug exposure-related TMA. * Presence or history of a condition that could trigger TMA, such as malignancy, bone marrow or organ transplant (other than kidney transplant) or autoimmune disease. * History of a kidney disease, other than aHUS. * History of Neisseria meningitidis infection within 6 months of study enrollment. * Known or suspected immune deficiency (e.g., history of frequent recurrent infections). * Positive HIV test. * Active systemic bacterial, viral, or fungal infection within 14 days before first crovalimab administration. * Presence of fever (\>= 38°C) before the first crovalimab administration (If fevers are solely due to the underlying aHUS pathology, and there is no evidence or suspicion of a systemic infection, participants may enroll). * Multi-system organ dysfunction or failure. * Recent intravenous immunoglobulin (IVIg) treatment. * Pregnant or breastfeeding or intending to become pregnant. * Participation in another interventional treatment study with an investigational agent or use of any experimental therapy within 28 days of screening or within five half lives of that investigational product, whichever is greater. * Recent use of tranexamic acid. * Current or previous treatment with a complement inhibitor (for Naive Cohort only). * First initiation of plasma exchange/plasma infusions (PE/PI) should not be more than 28 days prior to first crovalimab administration (for Naive Cohort only). * Last PE/PI completed less than 2 hours prior to first crovalimab administration (for Naive Cohort only). * Receiving PE/PI within 8 weeks of the first crovalimab administration (Switch Cohort only). * Normalization of serum creatinine values at baseline (\<97.5th percentile for age), (for Naive Cohort only). * Positive for active Hepatitis B and/or C infections (HBV/HCV) (for Switch Cohort and switching C5 SNP Pretreated Cohort participants who recently received C5 inhibitor treatment). * Cryoglobulinemia at screening (for Switch Cohort and C5 SNP Cohort participants who recently received C5 inhibitor treatment). * Diagnosis of a condition leading to non-aHUS TMA: Thrombotic Thrombocytopenic Purpura (TTP), Shiga Toxin producing Escherichia Coli (STEC)-TMA, Pneumococcal HUS, TMA secondary to cobalamin C defect (as demonstrated by either increased total blood homocysteine levels or MMACHC gene mutation) and TMA related to Diacylglycerol kinase ε (DGKE) nephropathy.

Primary outcome measure(s)

  • Naïve Cohort: Percentage of Participants With Complete Thrombotic Microangiopathy Response (cTMAr) Anytime From Baseline to Week 25 (After 24 Weeks on Treatment) — From baseline up to Week 25
    cTMAr was defined by meeting all of the following criteria at two separate assessments, obtained at least 4 weeks (a minimum of 26 days) apart, and any measurement in between: Platelet count ≥ lower limit of normal (LLN); Lactate dehydrogenase (LDH) ≤ upper limit of normal (ULN); and ≥ 25% decrease in serum creatinine from baseline. Participants with normalized creatinine (i.e., LLN ≤ creatinine ≤ ULN) at baseline were excluded from analysis. 95% confidence interval (CI) was calculated using Wilson's score method. Percentage has been rounded off.

Trial sites (20)

FacilityCityRegionStatus
Children's Hospital Colorado Aurora Colorado
University of Nebraska Omaha Nebraska
Hackensack University Medical Center Hackensack New Jersey
UZ Gent Ghent Belgium
UZ Leuven Gasthuisberg Leuven Belgium
Inst. Da Criança- Faculdade de Medicina Usp São Paulo São Paulo
CHU Sainte-Justine Montreal Quebec
Peking University First Hospital Beijing China
Beijing Children's Hospital, Capital Medical University Beijing China
The children's hospital , Zhejiang university school of medicine Hangzhou China
Hôpital Arnaud de Villeneuve Montpellier France
Gh Necker Enfants Malades Paris France
Institute of Kidney Diseases and Research Centre Ahmedabad Gujarat
Medanta-The Medicity Gurgaon Haryana
All India Institute Of Medical Sciences (AIIMS) New Delhi National Capital Territory of Delhi
Aichi Children?s Health and Medical Center Aichi Japan
Chiba Children's Hospital Chibashi, Chibaken Japan
Hospital de Especialidades Puerta de Hierro S.A de C.V. Zapopan Mexico
Uniwersyteckie Centrum Kliniczne Gdansk Poland
Instytut ?Centrum Zdrowia Matki Polki Lodz Poland
Official registry record

This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.

View NCT04958265 on ClinicalTrials.gov ↗ ← All trials in France