Status
Study
Lead sponsor
Phase
Enrol
US states
Start
Not yet open
Sarepta Therapeutics, Inc.
Phase 4
20
Texas
2026-08-31
Recruiting
Solid Biosciences Inc.
Phase 3
80
Arkansas, Texas, Virginia
2025-10-22
Active, closed
Hoffmann-La Roche
Phase 2
30
Arkansas, California, Georgia, Michigan, Texas, Virginia
2025-04-04
Active, closed
MED Institute Inc.
Phase 2
35
Texas
2024-08-05
By invitation
REGENXBIO Inc.
Observational
66
Arkansas, California, Illinois, Texas, Virginia
2024-05-08
Active, closed
Avidity Biosciences, Inc.
Phase 2
39
Arkansas, California, Georgia, Massachusetts, Minnesota, North Carolina, Ohio, Texas
2024-01-22
Recruiting
Sarepta Therapeutics, Inc.
Phase 1
83
Arkansas, California, Florida, Illinois, Missouri, North Carolina, Ohio, Texas
2020-11-23