Long Term Follow-up for RGX-202
Condition(s) studied
Investigational drug(s) / intervention(s)
No Intervention: Observational study
Study summary
RGX-202-5101 is a long-term follow up study that evaluates the long-term safety and efficacy of RGX-202 in participants who have received RGX-202 (an investigative gene therapy designed to deliver a transgene for novel microdystrophin that includes functional elements of naturally-occurring dystrophin including the C-Terminal (CT) domain) in a separate parent study.
Eligibility
Primary outcome measure(s)
- Evaluation of long-term safety of RGX-202 — Baseline, 5 years inclusive of parent study
Incidences of AEs and SAEs over time
Trial sites (5)
| Facility | City | Region | Status |
|---|---|---|---|
| Arkansas Children's Hospital | Little Rock | Arkansas | |
| Stanford School of Medicine /Division of Neuromuscular Medicine | Palo Alto | California | |
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago | Illinois | |
| The University of Texas Southwestern Medical Center | Dallas | Texas | |
| Virginia Commonwealth University | Richmond | Virginia |
More REGENXBIO Inc. trials in the USA
Other trials for the same condition
This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.
View NCT06491927 on ClinicalTrials.gov ↗ ← All trials in the USA