Status
Study
Lead sponsor
Phase
Enrol
US states
Start
Recruiting
MavriX Bio, LLC
Phase 1/2
12
California, Illinois, Massachusetts
2025-10-29
Recruiting
Ionis Pharmaceuticals, Inc.
Phase 3
158
California, Colorado, District of Columbia, Florida, Georgia, Illinois, Massachusetts, Missouri
2025-06-10
Active, closed
Ultragenyx Pharmaceutical Inc
Phase 3
129
California, Colorado, Florida, Georgia, Illinois, Massachusetts, Missouri, New York
2024-12-03
Active, closed
Ultragenyx Pharmaceutical Inc
Phase 3
255
California, Georgia, Illinois, Massachusetts, New York
2024-07-31
Active, closed
Ionis Pharmaceuticals, Inc.
Phase 1/2
71
California, Colorado, Illinois, Massachusetts, North Carolina, Texas
2021-12-22