Status
Study
Lead sponsor
Phase
Enrol
US states
Start
Recruiting
QED Therapeutics, a BridgeBio company
Phase 2
77
California, Maryland, Wisconsin
2025-11-19
Recruiting
Ascendis Pharma A/S
Phase 2
72
Minnesota, Texas, Wisconsin
2024-01-23
By invitation
Ascendis Pharma Growth Disorders A/S
Phase 2/3
140
Arkansas, Colorado, Delaware, Minnesota, Montana, New York, Texas, Wisconsin
2023-06-21
Recruiting
BioMarin Pharmaceutical
Observational
170
California, Maryland, North Carolina, Ohio, South Dakota, Texas, Wisconsin
2023-02-21
By invitation
QED Therapeutics, a BridgeBio company
Phase 2
300
California, Colorado, Delaware, Maryland, Missouri, Ohio, Tennessee, Wisconsin
2021-12-06
Active, closed
BioMarin Pharmaceutical
Phase 2
73
California, Delaware, Georgia, Illinois, Ohio, Tennessee, Texas, Wisconsin
2019-06-12