Status
Study
Lead sponsor
Phase
Enrol
US states
Start
Recruiting
Ionis Pharmaceuticals, Inc.
Phase 1/2
32
Michigan, Minnesota, North Carolina, Tennessee, Washington
2026-05-21
Recruiting
Stoke Therapeutics, Inc
Phase 3
170
Arizona, Arkansas, California, Colorado, District of Columbia, Florida, Illinois, Massachusetts
2025-06-04
Recruiting
Longboard Pharmaceuticals
Phase 3
104
Arkansas, California, Colorado, District of Columbia, Florida, Georgia, Illinois, Maryland
2024-09-25
Active, closed
UCB BIOSCIENCES, Inc.
Phase 3
25
Tennessee, Texas, Washington
2024-05-21
Recruiting
Encoded Therapeutics
Phase 1/2
47
California, Colorado, Florida, Illinois, Massachusetts, Michigan, Minnesota, North Carolina
2024-05-14
Active, closed
Jazz Pharmaceuticals
Phase 4
154
Arkansas, California, Florida, Georgia, Kansas, Kentucky, Maryland, Massachusetts
2021-07-07
Active, closed
Stoke Therapeutics, Inc
Phase 2
60
California, Colorado, District of Columbia, Florida, Illinois, Iowa, Massachusetts, Michigan
2021-01-20
Recruiting
Epygenix
Phase 3
150
Alabama, Arkansas, California, Connecticut, Delaware, Florida, Georgia, Illinois
2020-09-15