Congenital Myasthenic Syndrome Trials in the USA

Every industry-sponsored study on the ClinicalTrials.gov registry that lists a US site and is open, about to open, active-but-closed, or enrolling by invitation. This deliberately excludes academic and other non-industry sponsors — the full US registry across all sponsors runs to over 22,000 recruiting studies alone.

Download CSV

Source: ClinicalTrials.gov. Complete coverage of the industry-sponsored slice — all 9094 matching records are in this view (non-industry sponsors are out of scope by design, not truncated). Synced 17 Sep 2026, 08:23 UTC

9094

Studies in scope

industry-sponsored, all four open statuses

4935

Recruiting now

open to new participants

2188

Lead sponsors

across recruiting studies

Top states

California 2 Illinois 2 Massachusetts 1 Ohio 1 Pennsylvania 1

Narrow the registerReset

Search within results

Recruitment status

Phase

Lead sponsor

State

All 5 states

Target enrolment

Status

Study

Lead sponsor

Phase

Enrol

US states

Start

Active, closed

A Phase 1b Study to Investigate Safety and Tolerability of ARGX-119 in Adult Participants With DOK7-Congenital Myasthenic Syndromes (CMS)

NCT06436742Congenital Myasthenic Syndrome, CMS

argenx

Phase 1

California, Illinois

2024-09-24

Recruiting

A Natural History Study in Participants With Congenital Myasthenic Syndromes (CMS) Due to Mutations in DOK7, MUSK, AGRN, or LRP4

NCT06078553Congenital Myasthenic Syndrome

argenx

Observational

100

California, Illinois, Massachusetts, Ohio, Pennsylvania

2024-02-13

Cite this view

Priya Life Science (2026). Clinical trial register: industry-sponsored studies with a US investigative site, filtered. Derived from ClinicalTrials.gov. Retrieved 17 September 2026. https://priyalifescience.com/clinical-trials-usa/condition/congenital-myasthenic-syndrome

Query this register directly

GET /api/trials?country=usa&status=recruiting&format=json Try it now →

Listing here is informational and not medical advice; eligibility is determined by each study team. Compare pay for the teams running these studies in the US Pharma Salary Guide, see who's behind them in the US Company Directory, or track approvals on the FDA Approvals Tracker. For Irish, UK and EU sites, see the Ireland, UK and EU registers.