EN-374: Single dose of EN-374 administered by intravenous infusion after mobilization and followed by enrichment
Study summary
The goal of this clinical trial is to evaluate the safety and potential efficacy of the EN-374 treatment regimen and identify a dose level for further evaluation in participants with x-linked chronic granulomatous disease.
The main questions it aims to answer are:
* safety of the EN-374 treatment regimen
* effect of the EN-374 treatment regimen on the production of functional neutrophils with NADPH oxidase activity
Eligibility
Sex
MALE
Min age
3 Months
Max age
—
Healthy volunteers
No
Inclusion Criteria:
* Male
* ≥ 18 years of age during dose escalation, then ≥ 3 months of age during dose expansion
* Diagnosis of X-CGD with a pathogenic mutation in the CYBB gene
* History of at least 1 severe infection requiring medical intervention or chronic inflammatory disorder
* Does not have a suitable, available, and willing human leukocyte antigens (HLA)-matched (10/10) related donor
* Non-sterile male participants who are or may become sexually active with female partners of childbearing potential are required to use highly effective contraception
* Informed consent, with informed assent from capable participants
* Adequate organ function
Exclusion Criteria:
* Active bacteremia or fungemia
* History of human immunodeficiency virus (HIV), hepatitis B, or hepatitis C
* History or clinical evidence of any medical or social issues likely to put the participant at additional risk or to interfere with study conduct
* History of HSCT or granulocyte transfusions
* Known hypersensitivity to elements in the treatment regimen
* Undergone investigational gene therapy
* Treated with another investigational drug product within 30 days before screening
* Unable to comply with the visits and requirements of the protocol as determined by the Investigator
Primary outcome measure(s)
Safety of EN-374 — From start of mobilization until Month 12 Incidence rate across all age groups of:
* treatment-emergent adverse events (TEAEs)
* treatment-related TEAEs (TRAEs)
* serious adverse events (SAEs)
Trial sites (9)
Facility
City
Region
Status
University of California, Los Angeles
Los Angeles
California
University of California, San Francisco
San Francisco
California
Johns Hopkins All Children's Hospital
St. Petersburg
Florida
Boston Children's Hospital
Boston
Massachusetts
University of Minnesota
Minneapolis
Minnesota
Columbia University Irving Medical Center, Morgan Stanley Children's Hospital
This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.
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