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Clinical Trials in the UK / NCT06738017

Active, not recruiting Phase 1

Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants

NCT06738017 · tracked via the Priya Life Science UK tracker

Sponsor

BioMarin Pharmaceutical

Phase

Phase 1

Started

2025-02-21

Last updated

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Condition(s) studied

Alpha 1-Antitrypsin Deficiency

More BioMarin Pharmaceutical trials in the UK

An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia Active, not recruiting

A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months Recruiting

Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia Recruiting

A Multicenter Multinational Observational Study of Children With Hypochondroplasia Recruiting

A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401) Enrolling by invitation

Other trials for the same condition

A Study to Evaluate the Safety and Efficacy of BEAM-302 in Adult Patients With Alpha-1 Antitrypsin Deficiency (AATD) Recruiting

Long-term, Open-label Study of SAR447537 (INBRX-101) in Adults With Alpha-1 Antitrypsin Deficiency Emphysema Active, not recruiting

Official registry record

This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.

View NCT06738017 on ClinicalTrials.gov ↗ ← All trials in the UK