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Clinical Trials in the USA / NCT07287189
Recruiting Phase 2

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

NCT07287189 · tracked via the Priya Life Science USA tracker
Sponsor
Satellos Bioscience, Inc.
Phase
Phase 2
Started
2025-12-08
Last updated
2026-09-18

Condition(s) studied

Duchenne Muscular DystrophyDuchenneDMDNeuromuscular DiseasesMuscular Dystrophies

Investigational drug(s) / intervention(s)

SAT-3247Placebo

SAT-3247: SAT-3247 is a selective AAK1 inhibitor for oral tablet administration which promotes functional rescue of asymmetric satellite cell division, resulting in the robust production of muscle progenitor cells, subsequent improvement in muscle regeneration, and enhanced muscle function.

Placebo: matching placebo oral tablets

Study summary

Phase 2a trial of SAT-3247 in ambulatory DMD patients aged ≥ 7 and \< 10 years. The trial has two parts. In Part 1, the trial will study two doses of SAT-3247 in a randomized, double-blind, placebo-controlled weekday regimen for 12 weeks to determine the optimal dose, safety, tolerability, and preliminary efficacy. In Part 2, the trial will study two doses of SAT-3247 for an additional 9 months.

Eligibility

Sex
MALE
Min age
7 Years
Max age
9 Years
Healthy volunteers
No
Key Inclusion Criteria: * Has a definitive diagnosis of DMD based on documented clinical findings and prior genetic testing with a confirmed mutation in the DMD gene. * Male DMD patients who are ambulatory and aged ≥ 7 to \< 10 years at the time of screening. * Stable dose of systemic glucocorticoids (i.e., prednisolone, deflazacort, or vamorolone) according to the standard of care for ≥ 3 months prior to the Screening Visit and for the duration of the trial. Patients who are not receiving glucocorticosteroids are also eligible if stopped ≥ 3 months prior to the Screening Visit. * Stable doses of prescription medicines including ACE inhibitors, β-blockers, and diuretics (excluding glucocorticosteroids) and over-the-counter medicines and/or herbal supplements for supportive care ≥ 1 month prior to the Screening Visit and for the duration of the trial. * Participants that have previously received delandistrogene moxeparvovec (brand name Elevidys) either in a prior clinical trial or in the commercial setting \> 18 months prior to screening whose muscle function tests have stabilized or demonstrated decline ≥ 3 months prior to Screening, as determined by investigator and documented in chart notes, will be eligible. * Participants that have previously received an exon skipper \> 6 months prior to Screening whose muscle function tests have stabilized or demonstrated decline ≥ 3 months prior to Screening, as determined by investigator and documented in chart notes, will be eligible. * Participants receiving a stable dose of givinostat (brand name Duvyzat) for at least 18 months or longer prior to the Screening Visit will be eligible. Participants unable to tolerate givinostat who discontinued treatment before 18 months are eligible to enroll if date of last dose is ≥ 30 days from the Screening date. Givinostat should not be discontinued, if tolerated, to meet study entry criteria. * Participants that have received prior treatment with an investigational gene therapy product (other than delandistrogene moxeparvovec) ≥ 24 months prior to the Screening Visit. * If participating in a physical therapy/strength training regimen, must be stable for ≥ 2 months prior to the Screening Visit and for the duration of the trial. Key Exclusion Criteria: * Ambulatory patients expected to experience loss of ambulation within ≤ 12 months. * Participants for whom MRI or open muscle biopsy are contraindicated. * Evidence of significant hepatic dysfunction, defined as GLDH \> 2X upper limit of normal (ULN) at the Screening Visit. * Impaired cardiac function defined as a left ventricular ejection fraction of \< 50% on screening cardiac assessments (echocardiogram or MRI) or evidence of symptomatic cardiomyopathy. * A forced vital capacity \< 60% predicted at the Screening Visit. * Ongoing participation in any other therapeutic clinical trial or follow-up study for a therapeutic intervention * Consumption of grapefruit juice or grapefruit containing products * Severe behavioural or cognitive problems that preclude participation in the study, in the opinion of the investigator. Additional entry criteria will be reviewed with the clinical site investigator.

Primary outcome measure(s)

Trial sites (21)

FacilityCityRegionStatus
University of California Los Angeles Los Angeles California Recruiting
Colorado Children's Aurora Colorado Recruiting
Lurie Children's Chicago Illinois Recruiting
UMass Memorial Medical Center Worcester Massachusetts Recruiting
Washington University St Louis Missouri Recruiting
Nationwide Children's Hospital Columbus Ohio Recruiting
Seattle Children's Seattle Washington Recruiting
Children's Hospital at Westmead Westmead New South Wales Recruiting
Royal Children's Hospital Melbourne Melbourne Victoria Recruiting
Hôpital De La Citadelle (CHR) Liège Liège Recruiting
UZ Gent Ghent Oost-Vlaanderen Recruiting
Children's Hospital Eastern Ontario Ottawa Ontario Recruiting
Klinika Neurologii Rozwojowej Uniwersyteckie Gdansk Pomeranian Voivodeship Recruiting
Instytut Centrum Zdrowia Matki Polki Lodz Łódź Voivodeship Recruiting
Clinic of Neurology and Psychiatry for Children and Youth Belgrade Serbia Not Yet Recruiting
University Children's Clinic Tirsova Belgrade Serbia Recruiting
Mother and Child Health Care Institute Belgrade Serbia Recruiting
Hospital Universitario Donostia Donostia / San Sebastian Basque Country Not Yet Recruiting
Hospital Universitario y Politécnico La Fe Valencia Valencia Recruiting
Hospital Infantil i Hospital de la Dona Barcelona Spain Recruiting
Great Ormond Street London UK Recruiting

Other trials for the same condition

Official registry record

This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.

View NCT07287189 on ClinicalTrials.gov ↗ ← All trials in the USA