SAT-3247: SAT-3247 is a selective AAK1 inhibitor for oral tablet administration which promotes functional rescue of asymmetric satellite cell division, resulting in the robust production of muscle progenitor cells, subsequent improvement in muscle regeneration, and enhanced muscle function.
Placebo: matching placebo oral tablets
Study summary
Phase 2a trial of SAT-3247 in ambulatory DMD patients aged ≥ 7 and \< 10 years. The trial has two parts. In Part 1, the trial will study two doses of SAT-3247 in a randomized, double-blind, placebo-controlled weekday regimen for 12 weeks to determine the optimal dose, safety, tolerability, and preliminary efficacy. In Part 2, the trial will study two doses of SAT-3247 for an additional 9 months.
Eligibility
Sex
MALE
Min age
7 Years
Max age
9 Years
Healthy volunteers
No
Key Inclusion Criteria:
* Has a definitive diagnosis of DMD based on documented clinical findings and prior genetic testing with a confirmed mutation in the DMD gene.
* Male DMD patients who are ambulatory and aged ≥ 7 to \< 10 years at the time of screening.
* Stable dose of systemic glucocorticoids (i.e., prednisolone, deflazacort, or vamorolone) according to the standard of care for ≥ 3 months prior to the Screening Visit and for the duration of the trial. Patients who are not receiving glucocorticosteroids are also eligible if stopped ≥ 3 months prior to the Screening Visit.
* Stable doses of prescription medicines including ACE inhibitors, β-blockers, and diuretics (excluding glucocorticosteroids) and over-the-counter medicines and/or herbal supplements for supportive care ≥ 1 month prior to the Screening Visit and for the duration of the trial.
* Participants that have previously received delandistrogene moxeparvovec (brand name Elevidys) either in a prior clinical trial or in the commercial setting \> 18 months prior to screening whose muscle function tests have stabilized or demonstrated decline ≥ 3 months prior to Screening, as determined by investigator and documented in chart notes, will be eligible.
* Participants that have previously received an exon skipper \> 6 months prior to Screening whose muscle function tests have stabilized or demonstrated decline ≥ 3 months prior to Screening, as determined by investigator and documented in chart notes, will be eligible.
* Participants receiving a stable dose of givinostat (brand name Duvyzat) for at least 18 months or longer prior to the Screening Visit will be eligible. Participants unable to tolerate givinostat who discontinued treatment before 18 months are eligible to enroll if date of last dose is ≥ 30 days from the Screening date. Givinostat should not be discontinued, if tolerated, to meet study entry criteria.
* Participants that have received prior treatment with an investigational gene therapy product (other than delandistrogene moxeparvovec) ≥ 24 months prior to the Screening Visit.
* If participating in a physical therapy/strength training regimen, must be stable for ≥ 2 months prior to the Screening Visit and for the duration of the trial.
Key Exclusion Criteria:
* Ambulatory patients expected to experience loss of ambulation within ≤ 12 months.
* Participants for whom MRI or open muscle biopsy are contraindicated.
* Evidence of significant hepatic dysfunction, defined as GLDH \> 2X upper limit of normal (ULN) at the Screening Visit.
* Impaired cardiac function defined as a left ventricular ejection fraction of \< 50% on screening cardiac assessments (echocardiogram or MRI) or evidence of symptomatic cardiomyopathy.
* A forced vital capacity \< 60% predicted at the Screening Visit.
* Ongoing participation in any other therapeutic clinical trial or follow-up study for a therapeutic intervention
* Consumption of grapefruit juice or grapefruit containing products
* Severe behavioural or cognitive problems that preclude participation in the study, in the opinion of the investigator.
Additional entry criteria will be reviewed with the clinical site investigator.
Primary outcome measure(s)
Safety of SAT-3247 — 12 weeks in Part 1 and up to 12 months in part 2 Occurrence of treatment emergent adverse events and relationship to investigational product
Tolerability of SAT-3247 — 12 weeks in Part 1 and up to 12 months in Part 2 occurrence of clinically significant changes in physical exam, clinical laboratory measures, vital signs, and ECG
SAT-3247 effects on muscle strength — 12 weeks in Part 1 and up to 12 months in Part 2 change from baseline in muscle force as determined by dynamometry
Trial sites (21)
Facility
City
Region
Status
University of California Los Angeles
Los Angeles
California
Recruiting
Colorado Children's
Aurora
Colorado
Recruiting
Lurie Children's
Chicago
Illinois
Recruiting
UMass Memorial Medical Center
Worcester
Massachusetts
Recruiting
Washington University
St Louis
Missouri
Recruiting
Nationwide Children's Hospital
Columbus
Ohio
Recruiting
Seattle Children's
Seattle
Washington
Recruiting
Children's Hospital at Westmead
Westmead
New South Wales
Recruiting
Royal Children's Hospital Melbourne
Melbourne
Victoria
Recruiting
Hôpital De La Citadelle (CHR)
Liège
Liège
Recruiting
UZ Gent
Ghent
Oost-Vlaanderen
Recruiting
Children's Hospital Eastern Ontario
Ottawa
Ontario
Recruiting
Klinika Neurologii Rozwojowej Uniwersyteckie
Gdansk
Pomeranian Voivodeship
Recruiting
Instytut Centrum Zdrowia Matki Polki
Lodz
Łódź Voivodeship
Recruiting
Clinic of Neurology and Psychiatry for Children and Youth
This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.
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