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Clinical Trials in the USA / NCT07282847
Recruiting Phase 1/2

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

NCT07282847 · tracked via the Priya Life Science USA tracker
Sponsor
AskBio Inc
Phase
Phase 1/2
Started
2026-04-15
Last updated
2026-07-20

Condition(s) studied

Pompe Disease (Late-onset)Pompe Disease Late-OnsetLOPD

Investigational drug(s) / intervention(s)

AB-1009 (GAA Gene)

AB-1009 (GAA Gene): A single intravenous infusion of AB-1009

Study summary

This is a single-arm, open-label, dose-escalation study to evaluate the safety, tolerability and efficacy of a single intravenous infusion of AB-1009 in adult participants with late-onset Pompe disease (LOPD).

Eligibility

Sex
ALL
Min age
18 Years
Max age
65 Years
Healthy volunteers
No
Inclusion Criteria: 1. Participant must be ≥18 to ≤65 years of age at the time of signing the informed consent form. 2. Confirmed GAA enzyme deficiency from any tissue source and/or confirmed biallelic GAA gene mutations. 3. Undergone enzyme replacement treatment (ERT) (either alglucosidase alfa (Lumizyme®), avalglucosidase alfa-ngpt (Nexviazyme®)), or cipaglucosidase alfa (Pombiliti®) for at least 6 months (at least 10 infusions) before signing the initial informed consent form. During the screening process, participants need to remain on their current ERT until close to dosing; 4. FVC in the upright position ≥30% and ≤80% of predicted; 5. Capable of walking at least 100 meters in the 6MWT (use of a cane, quad cane, or standard walker is permitted); 6. Male or female. Contraceptive/barrier use by men and women requirements as per protocol. 7. Capable of giving informed consent. 8. Able to understand and comply with all study procedures. Exclusion Criteria: 1. Severe cardiomyopathy, defined as left ventricular ejection fraction (LVEF) \<40% or New York Heart Association (NYHA) functional class 3 or above; 2. Require invasive mechanical ventilation, or rely on noninvasive ventilation during the day; 3. Intolerance to ERT or investigator-assessed intolerance to ERT, prior experience of serious ERT-related infusion-associated reactions (IARs); 4. Have known intrinsic liver diseases, including hepatitis, HIV-related liver disease, prior diagnosis of portal hypertension, splenomegaly, hepatic encephalopathy, severe fatty liver, cirrhosis or liver fibrosis ≥stage 2, ultrasound-identified liver neoplasms, or laboratory tests suggesting elevated alpha-fetoprotein. Patients with liver function tests including ALT or AST \>3× upper limit of normal (ULN) or any total bilirubin above ULN during screening will also be excluded; 5. Prior or ongoing medical condition(s), including any active infection, malignancy within 5 years of screening (except basal or squamous cell skin cancer), physical finding(s), assessment findings, or laboratory abnormality that, in the investigator's opinion, would impact participant's safety and compliance with the study procedures. 6. Have received gene therapy prior to screening; 7. Have received any systemic immunosuppressants (except inhalation or topical use) other than glucocorticoids 30 days prior to screening through completion of screening through completion of screening, and/or known intolerance to immunosuppressants such as glucocorticoids; other concomitant immunosuppression would require sponsor approval. 8. Use of investigational drugs or drugs that could affect this study as evaluated by the investigator within 30 days prior to screening through completion of Week 52 or within 5 half-lives of the investigational drug (whichever is longer); 9. Have received any vaccine within 30 days prior to dosing; 10. Other conditions that make the participant not eligible for the study according to the investigator. 11. Contraindication to MRI, hypersensitivity to contrast dyes, shellfish, or iodine, or implanted spinal rods, cardiac pacemaker, or other implantation that would distort cMRI images.

Primary outcome measure(s)

Trial sites (9)

FacilityCityRegionStatus
Barrow Neurological Institute Phoenix Arizona Not Yet Recruiting
University of California, Irvine (UCI) Irvine California Recruiting
Stanford Neuroscience Health Center Palo Alto California Not Yet Recruiting
NYU Langone New York New York Not Yet Recruiting
Duke University Durham North Carolina Recruiting
Hospital of the University of Pennsylvania Philadelphia Pennsylvania Recruiting
University of Pittsburgh Medical Center (UPMC) Pittsburgh Pennsylvania Not Yet Recruiting
University of Texas Southwest Medical Center Dallas Texas Recruiting
Virginia Commonwealth University (VCU) Richmond Virginia Not Yet Recruiting

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Official registry record

This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.

View NCT07282847 on ClinicalTrials.gov ↗ ← All trials in the USA