Ireland
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Recruiting Phase 2/3

A Sequential Phase 2/3 Study of APL2 in Patients With Focal Segmental Glomerulosclerosis

NCT07213960 · tracked via the Priya Life Science USA tracker
Phase
Phase 2/3
Started
2026-12
Last updated
2026-09-02

Condition(s) studied

FSGS

Investigational drug(s) / intervention(s)

APL2Placebo

APL2: Complement (C3) Inhibitor

Placebo: Sterile solution of equal volume to active arm

Study summary

This is a sequential phase 2/3 study to evaluate the efficacy and safety of twice-weekly subcutaneous (SC) infusions of APL2 in patients diagnosed with FSGS. The initial phase 2 portion is a single-arm, open-label study in adults diagnosed with FSGS. Phase 2 will commence prior to randomizing for phase 3. The phase 3 portion of the study is a randomized, placebo-controlled, double-blinded, multicenter study in adults and adolescents diagnosed with FSGS.

Eligibility

Sex
ALL
Min age
18 Years
Max age
—
Healthy volunteers
No
Inclusion Criteria: * Age * Phase 2: adults aged ≥18 years * Phase 3: adults aged ≥18 years; if and where approved, adolescents (aged 12--17 years) at the time of signing the informed consent and assent form * Weight ≥30 kg and ≤100 kg at screening * FSGS diagnosis * Phase 2: primary, genetic, or undetermined FSGS diagnosed by kidney biopsy * Phase 3: primary, genetic, or undetermined FSGS diagnosed by kidney biopsy or by recognized podocyte genetic mutation * At least 1.5 g/day of proteinuria on a screening 24-hour urine collection and a uPCR of at least 1.5 g/g in at least 2 FMU samples collected during screening * Estimated glomerular filtration rate (eGFR) ≥25 mL/min/1.73 m2 * Stable regimen for FSGS treatment for at least 12 weeks prior to randomization, with no planned or anticipated adjustments or dose changes to the stable treatment regimen Exclusion Criteria: * Previous exposure to APL2 * Evidence of improving kidney disease in the 8 weeks prior to screening or during the screening period according to available data * FSGS secondary to another condition (eg, infectious, diabetic, drug-induced, obesity, prematurity, sickle-cell, vesicoureteral reflux, congenital anomalies of the kidney, and urinary tract) * Type 1 or uncontrolled (HbA1C ≥8%) type 2 diabetes mellitus * History of kidney transplant * Current or prior diagnosis of HIV, hepatitis B, or hepatitis C infection or positive serology or viral load during screening that is indicative of active infection with any of these viruses * Hypersensitivity to APL2 or to any of the excipients * Significant other kidney disease that would, in the opinion of the investigator, confound interpretation of study results * Use of rituximab, belimumab, or any approved or investigational anticomplement therapy within 5 half-lives of that product prior to the screening period

Primary outcome measure(s)

  • Phase 2: Evaluate the efficacy of APL2 in terms of change from baseline in log-transformed urine protein to creatinine ratio (uPCR) — Baseline to Week 12
    Change from Baseline in Log-Transformed uPCR will be based on triplicate first morning urine (FMU)
  • Phase 3: Change from baseline in log-transformed urine protein to creatinine ratio (uPCR) — Baseline to Week 52
    Change from baseline in log-transformed uPCR will be based on triplicate first morning urine (FMU)

Trial sites (2)

FacilityCityRegionStatus
Investigator Site 1 Chicago Illinois Recruiting
Investigator Site 2 New York New York Recruiting
Official registry record

This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.

View NCT07213960 on ClinicalTrials.gov ↗ ← All trials in the USA