Recruiting
Phase 1/2
A Study Assessing HMB-002 in Participants With Von Willebrand Disease
Condition(s) studied
Von Willebrand Disease (VWD)Von Willebrand Disease (VWD), Type 1Von Willebrand Disease (VWD), Type 2Von Willebrand Disease (VWD), Type 3
Investigational drug(s) / intervention(s)
HMB-002 (Part A)HMB-002 (Part B)HMB-002 with Concomitant Factor Concentrate (Part C) (Not Applicable in US)
HMB-002 (Part A): HMB-002 will be administered subcutaneously. Part A will utilize sentinel dosing. The planned duration of study participants in Part A is approximately 12 weeks.
HMB-002 (Part B): HMB-002 will be administered subcutaneously. Part B dosing intervals will be determined following evaluation of Part A results. The planned duration of study participants in Part B will be approximately 21 weeks.
HMB-002 with Concomitant Factor Concentrate (Part C) (Not Applicable in US): HMB-002 will be administered as a single dose with a concomitant single dose of factor concentrate. The planned duration of study participants in Part C will be approximately 17 weeks.
Study summary
This is a first-in-human (FIH), Phase 1/2, 3-part open-label, dose escalation, safety, tolerability, pharmacokinetic (PK), pharmacodynamic (PD), and efficacy study evaluating HMB-002 in participants with VWD. Part A of the study involves a single ascending dose (SAD) regimen design to establish safety, tolerability, PK, and PD effect. In Part B of the study, the safety and tolerability of repeat dosing will be established prior to cohort expansion to explore efficacy. Part C will evaluate the safety, PK, and PD of a single concomitant dose of HMB-002 and factor concentrate with Type 3 VWD or Type 1 VWD with low residual VWF and FVIII who use factor concentrate as prophylaxis.
Eligibility
Key Inclusion Criteria:
1. Weight 50 to 120 kg, inclusive.
2. Documented diagnosis of Congenital VWD, confirmed by laboratory testing consistent with ISTH/ASH) diagnostic guidelines).
3. Vital signs are within normal ranges at Screening.
4. Participants must meet the following baseline organ function, indicated by laboratory criteria as Screening:
1. Renal: Estimated glomerular filtration rate (eGFR) of ≥45 mL/min/1.73m\^2.
2. Hepatic: Aspartate aminotransferase (AST), alanine aminotransferase (ALT), and total bilirubin ≤1.5 upper limit of normal (ULN) at Screening. For participants with a history of Gilbert's Syndrome, total bilirubin ≤2 × ULN.
3. Hematology \>85 g/L and platelet count \>120 x 10\^9/L.
Part A Only:
5. Age: ≥18 and \<70 years of age at the time of informed consent.
6. VWD Subtype Eligibility:
* Cohorts A1 and A2: Participants with Type 1 VWD, only.
* Cohorts A3 and A4: Participants with Type 1 VWD (including Type 1C) and Type 2A VWD
7. Residual VWF activity of ≤ 50 IU/dL and FVIII activity ≤ 70 IU/dL during screening.
Part B Only:
8. Age: ≥16 and \<70 years of age at the time of informed consent.
9. VWD Subtype Eligibility: Participants with Type 1 VWD (including Type 1C) and Type 2A.
10. Residual VWF activity of ≤50 IU/dL and FVIII activity ≤70 IU/dL during screening.
11. Symptomatic Disease: Participants must be symptomatic, typically reporting bleeding events on a monthly basis.
12. Bleeding History (must meet one of the following):
1. Prior Observational Study Participation:
The participant must have participated in the observational study HMB-002-101\_SCR (VELORA Discover), have a minimum annualized treated bleeding event (ATBR) of 3; OR
2. Medical Record-Documented Bleeding History:
The Investigator confirms that ≥3 treated bleeding events have been documented in the participant's medical record within the preceding 12 months.
Part C Only:
13. Age: ≥18 and \<70 years of age at the time of informed consent.
14. Participants with Type 3 VWD or Type 1 VWD with low residual VWF and FVIII activity levels (VWF activity \<5 IU/dL and FVIII activity \<10 IU/dL).
15. Receives regular VWF concentrate (at least 1/week) as part of their routine care (usual dose ≤50 IU/kg).
Key Exclusion Criteria:
1. Personal history of venous or arterial thrombosis or thromboembolic disease, except for catheter-associated, superficial venous thrombosis.
2. High risk thrombophilia: Homozygous Factor V Leiden (FVL), compound heterozygous FVL/Prothrombin gene mutation, Antithrombin deficiency with activity \<50%. Congenital Protein C and Protein S deficiency with levels \<50%.
3. Body mass index (BMI) \>35 kg/m\^2 (obese, adjusted for ethnicity).
4. Presence of other conditions that substantially increase risk of thrombosis either individually (for participants \>65 years of age) or in combination (for participants ≤65 years of age), at the discretion of the Investigator or Medical Monitor.
5. Clinically significant cardiovascular disease.
6. Other known severe bleeding disorder(s) other than VWD.
7. Requirement for concomitant medications that affect hemostasis (including, but not limited to anticoagulation, antiplatelet agents, certain non-steroidal anti-inflammatory drugs) and cannot refrain from use for 14 days prior to the first dose of study drug and throughout the study.
Exclusion Criteria for Part A and Part B Only
8. Requirement for ongoing hemostatic treatment to prevent bleeding (bleed prophylaxis). Prophylaxis administered intermittently for procedures or surgery to reduce bleeding risk is permitted.
Primary outcome measure(s)
- Incidence of Treatment emergent adverse events (TEAE) — up to Day 113
Trial sites (25)
| Facility | City | Region | Status |
| Phoenix Children's Hospital |
Phoenix |
Arizona |
Not Yet Recruiting |
| Arkansas Children's Hospital |
Little Rock |
Arkansas |
Not Yet Recruiting |
| Children's Hospital of Los Angeles |
Los Angeles |
California |
Not Yet Recruiting |
| University of Miami Hospital and Clinics, Sylvester Comprehensive Cancer Center |
Miami |
Florida |
Not Yet Recruiting |
| Emory Children's Center |
Atlanta |
Georgia |
Not Yet Recruiting |
| Innovative Hematology, Inc./Indiana Hemophilia and Thrombosis Center |
Indianapolis |
Indiana |
Recruiting |
| Tulane University School of Medicine |
New Orleans |
Louisiana |
Not Yet Recruiting |
| University of Michigan Hospitals, Department of Hemophilia and Coagulation Disorders |
Ann Arbor |
Michigan |
Not Yet Recruiting |
| Mayo Clinic - Rochester |
Rochester |
Minnesota |
Not Yet Recruiting |
| Oregon Health & Science University |
Portland |
Oregon |
Not Yet Recruiting |
| Hemophilia Center of Western Pennsylvania |
Pittsburgh |
Pennsylvania |
Not Yet Recruiting |
| The University of Texas Southwestern Medical Center |
Dallas |
Texas |
Not Yet Recruiting |
| Washington Institute For Coagulation (WIC) |
Seattle |
Washington |
Not Yet Recruiting |
| Fiona Stanley Hospital |
Murdoch |
Perth |
Not Yet Recruiting |
| Royal Prince Alfred Hospital |
Camperdown |
Sydney |
Recruiting |
| The Alfred Hospital |
Melbourne |
Victoria |
Recruiting |
| Basingstoke and North Hampshire Hospital |
Basingstoke |
Hampshire |
Recruiting |
| St George's Hospital |
Tooting |
London |
Not Yet Recruiting |
| Royal London Hospital |
Whitechapel |
London |
Not Yet Recruiting |
| University Hospitals Birmingham NHS Foundation Trust |
Birmingham |
United Kingdom |
Not Yet Recruiting |
| University Hospital of Wales |
Cardiff |
United Kingdom |
Recruiting |
| St James's University Hospital, Leeds Haemophilia Centre |
Leeds |
United Kingdom |
Not Yet Recruiting |
| Royal Liverpool and Broadgreen University Hospitals NHS TRUST, The Roald Dahl Haemostasis and Thrombosis Centre |
Liverpool |
United Kingdom |
Not Yet Recruiting |
| Richmond Pharmacology |
London |
United Kingdom |
Recruiting |
| St Thomas' Hospital |
London |
United Kingdom |
Not Yet Recruiting |