Vosoritide: Subcutaneous injection of recommended dose of vosoritide based on weight-band dosing once daily.
Placebo: Subcutaneous injection of recommended dose of placebo
Study summary
The intent and design of this Phase 3 study is to assess vosoritide as a therapeutic option for the treatment of children with hypochondroplasia (HCH).
Eligibility
Sex
ALL
Min age
3 Years
Max age
17 Years
Healthy volunteers
No
Inclusion Criteria:
1. Participants must be ≥ 3 to \< 18 years of age at enrollment
2. A confirmed genetic diagnosis of HCH
3. A height Z score of ≤ - 2.0 standard deviations (SDs) in reference to the general population of the same age and sex, as calculated using the Center for Disease Control and Prevention (CDC) growth charts
4. Males and females are eligible to participate in this clinical study.
5. Females ≥ 10 years old or who have begun menses must have a negative pregnancy test at the Screening Visit and be willing to have additional pregnancy tests during the study.
6. If sexually active, participants must be willing to use a highly effective method of contraception while participating in the study.
Exclusion Criteria:
1. Short stature condition other than HCH
2. Have an unstable condition likely to require surgical intervention during the study.
3. Evidence of decreased growth velocity and/or growth plate closure
4. Taking any of the prohibited medications
5. Treated with growth hormone, insulin-like growth factor 1 (IGF-1), or anabolic steroids
6. Planned or expected to have limb-lengthening surgery during the study period.
7. Planned or expected bone-related surgery (ie, surgery involving disruption of bone cortex, excluding tooth extraction), during the study period
8. Require any investigational agent prior to completion of study period.
9. Received vosoritide or another investigational product or investigational medical device in the past
10. Have used any investigational product or investigational medical device for the treatment of HCH or short stature at any time, including vosoritide
11. Have current malignancy, history of malignancy, or currently under work-up for suspected malignancy.
12. Have known hypersensitivity to vosoritide or its excipients.
13. Concurrent disease or condition that, in the view of the investigator, would interfere with study participation or safety evaluations, for any reason.
Primary outcome measure(s)
Change from baseline in annualized growth velocity (AGV) at Week 52 versus placebo — At week 52
Trial sites (23)
Facility
City
Region
Status
Nemours Alfred I. DuPont Hospital for Children
Wilmington
Delaware
Children's National Medical Center
Washington D.C.
District of Columbia
Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago
Illinois
Medical College of Wisconsin
Milwaukee
Wisconsin
Murdoch Children's Research Institute
Parkville
Victoria
University of Alberta Stollery Children's Hospital
Edmonton
Alberta
SickKids - The Hospital for Sick Children
Toronto
Ontario
Centre Hospitalier Universitaire Sainte-Justine
Montreal
Quebec
Hospices Civils de Lyon - Hopital Femme Mere Enfant
This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.
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