Delandistrogene Moxeparvovec: No study medication will be provided by the sponsor during this study.
Standard of Care: No study medication will be provided by the sponsor during this study.
This is a multicenter, prospective, observational Phase 4 study including a post marketing safety requirement, designed to collect both medical history data and prospective data on Duchenne muscular dystrophy (DMD) treatment outcomes in participants receiving delandistrogene moxeparvovec (ELEVIDYS) as part of clinical care, compared to participants with DMD receiving or prescribed to start chronic glucocorticoid treatment at the time of study enrollment in routine clinical practice.
| Facility | City | Region | Status |
|---|---|---|---|
| Arkansas Children's Hospital | Little Rock | Arkansas | |
| Children's Hospital Los Angeles - PIN | Los Angeles | California | |
| University of Colorado - PPDS | Aurora | Colorado | |
| Connecticut Children's Medical Center - Hartford | Hartford | Connecticut | |
| Children's National Medical Center | Washington D.C. | District of Columbia | |
| Nicklaus Children's Hospital | Miami | Florida | |
| Nemours Children's Hospital - Orlando | Orlando | Florida | |
| All Children's Research Institute, Inc | St. Petersburg | Florida | |
| Ann and Robert H Lurie Childrens Hospital of Chicago | Chicago | Illinois | |
| Indiana Clinical and Translational Science Institute | Indianapolis | Indiana | |
| University of Kansas Medical Center | Kansas City | Kansas | |
| University of Michigan | Ann Arbor | Michigan | |
| Duke Lenox Baker Children's Hospital | Durham | North Carolina | |
| Childrens Hospital Medical Center of Akron | Akron | Ohio | |
| OHSU Healthcare (Oregon Health and Science University) | Portland | Oregon | |
| Penn State Health Milton S. Hershey Medical Center | Hershey | Pennsylvania | |
| Children's Hospital of Philadelphia | Philadelphia | Pennsylvania | |
| Le Bonheur Children's Hospital | Memphis | Tennessee | |
| Vanderbilt University Medical Center | Nashville | Tennessee | |
| Cook Children's Hospital | Fort Worth | Texas | |
| University of Virginia | Charlottesville | Virginia | |
| Children's Hospital of the King's Daughters | Norfolk | Virginia | |
| Seattle Children's Hospital | Seattle | Washington | |
| The Board of Regents of the University of Wisconsin | Madison | Wisconsin | |
| The Medical College of Wisconsin | Milwaukee | Wisconsin |
This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.
View NCT06270719 on ClinicalTrials.gov ↗ ← All trials in the USA