🇮🇪Ireland
16°C Partly Cloudy · Dublin
Live Updates
--:--:-- IST
Writer Login
Latest
Clinical Trials in the UK / NCT06760546
Recruiting Phase 3

A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756)

NCT06760546 · tracked via the Priya Life Science UK tracker
Sponsor
Rhythm Pharmaceuticals, Inc.
Phase
Phase 3
Started
2025-09-23
Last updated
2026-02-12

Condition(s) studied

Hypothalamic ObesityMultiple Pituitary Hormone Deficiency Genetic FormSepto-Optic DysplasiaOptic Nerve HypoplasiaChildhood-onset Combined Pituitary Hormone DeficiencyPituitary Stalk Interruption Syndrome

Investigational drug(s) / intervention(s)

SetmelanotidePlacebo

Setmelanotide: Solution for daily subcutaneous injection

Placebo: Placebo matched to setmelanotide for daily subcutaneous injection

Study summary

This is a sub-study of Study RM-493-040 (NCT05774756).

The goal of this sub-study is to learn how well Setmelanotide works to improve weight reduction, hunger, and quality of life in patients 4 years of age and older with congenital Hypothalamic Obesity (cHO). To determine how well setmelanotide works and how safe it is, patients with cHO will take a daily injection of either setmelanotide or placebo and complete trial assessments for up to 26 weeks on a therapeutic regimen.

Eligibility

Sex
ALL
Min age
4 Years
Max age
Healthy volunteers
No
Key Inclusion Criteria: 1. Diagnosis of multiple pituitary hormone deficiency (MPHD), or septo-optic dysplasia (SOD), or optic nerve hypoplasia (ONH), or Childhood-onset combined pituitary hormone deficiency (CPHD), or Pituitary Stalk Interruption Syndrome (PSIS) with at least one pituitary deficiency AND a body mass index (BMI) of ≥30 kg/m2 for patients ≥18 years of age, or BMI ≥95th percentile for age and sex for patients 4 to \<18 years 2. Age 4 years and older 3. Weight gain associated with the hypothalamic injury and a BMI of ≥30 kg/m2 for patients ≥18 years of age or BMI ≥95th percentile for age and sex for patients 4 to \<18 years of age 4. Agree to use a highly effective form of contraception throughout the study and for 90 days after the study Key Exclusion Criteria: 1. Diagnosis of Prader-Willi syndrome (PWS) or Rapid-onset obesity with hypoventilation, hypothalamic, autonomic dysregulation, neuroendocrine tumor syndrome (ROHHADNET) 2. Weight loss \>2% in the previous 3 months for patients aged ≥18 years or \>2% reduction in BMI for patients aged 4 to \<18 years 3. Bariatric surgery or procedure within last 2 years 4. Diagnosis of severe psychiatric disorders; any suicidal ideation, attempt or behavior 5. Current, clinically significant pulmonary, cardiac, metabolic, or oncologic disease 6. Significant dermatologic findings relating to melanoma or pre-melanoma skin lesions (excluding non-invasive basal or squamous cell lesion) 7. History or close family history of skin cancer or melanoma 8. Participation in any clinical trial with an investigational drug/device within 3 months prior to the first trial dose 9. Previously enrolled in a clinical trial involving setmelanotide or any previous exposure to setmelanotide 10. Inability to comply with once daily (QD) injection regimen 11. If female, pregnant and/or breastfeeding. 12. If receiving hormone replacement therapy, dose has remained stable for at least 2 months before Screening Other protocol defined Inclusion/Exclusion criteria may apply.

Primary outcome measure(s)

Trial sites (11)

FacilityCityRegionStatus
University of Alabama Birmingham Alabama Recruiting
Children's Hospital Colorado Aurora Colorado Recruiting
Lurie Children's Hospital Chicago Illinois Recruiting
Boston Children's Hospital Boston Massachusetts Recruiting
Children's Minnesota Saint Paul Minnesota Recruiting
Columbia University Irving Medical Center New York New York Recruiting
Children's Hospital of Philadelphia Philadelphia Pennsylvania Recruiting
Seattle Children's Research Institute Seattle Washington Recruiting
UCL Great Ormond Street Institute of Child Health London Greater London Recruiting
Birmingham Women and Children's Hospital NHS Trust Birmingham West Midlands Recruiting
Hull Royal Infirmary Hull United Kingdom Recruiting

More Rhythm Pharmaceuticals, Inc. trials in the UK

Other trials for the same condition

Official registry record

This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.

View NCT06760546 on ClinicalTrials.gov ↗ ← All trials in the UK