Sevasemten: Sevasemten is administered orally once per day
EDG-5506-203 MESA is an open-label extension study to assess the long-term effect of sevasemten (EDG-5506) on safety, biomarkers, and functional measures in adults and adolescents with Becker muscular dystrophy
| Facility | City | Region | Status |
|---|---|---|---|
| Arkansas Children's Hospital | Little Rock | Arkansas | |
| UC San Diego | La Jolla | California | |
| UCLA Medical Center | Los Angeles | California | |
| UC Irvine Medical Center | Orange | California | |
| Stanford Neuroscience Health Center | Palo Alto | California | |
| UC Davis Medical Center | Sacramento | California | |
| UC Denver | Aurora | Colorado | |
| University of Florida | Gainesville | Florida | |
| Rare Disease Research | Atlanta | Georgia | |
| Northwestern University | Chicago | Illinois | |
| Indiana University School of Medicine | Indianapolis | Indiana | |
| University of Iowa | Iowa City | Iowa | |
| University of Kansas Medical Center | Kansas City | Kansas | |
| Kennedy Krieger Institute | Baltimore | Maryland | |
| University of Massachusetts Memorial Medical Center | Worcester | Massachusetts | |
| Washington University School of Medicine | St Louis | Missouri | |
| University of Rochester Medical Center | Rochester | New York | |
| Rare Disease Research, LLC NC | Hillsborough | North Carolina | |
| University of Cincinnati Gardner Neuroscience Institute | Cincinnati | Ohio | |
| Nationwide Children's Hospital | Columbus | Ohio | |
| University of Pennsylvania | Philadelphia | Pennsylvania | |
| National Neuromuscular Research Institute | Austin | Texas | |
| Neurology Rare Disease Center | Denton | Texas | |
| Virginia Commonwealth University Health | Richmond | Virginia | |
| St Vincent's Hospital | Melbourne | Victoria | |
| University Hospital Gent | Ghent | Belgium | |
| Universitaire Ziekenhuizen Leuven | Leuven | Belgium | |
| Centre Hospitalier Régional de la Citadelle | Liége | Belgium | |
| Rigshospitalet | Copenhagen | Denmark | |
| Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone | Marseille | France | |
| CHU de Nantes | Nantes | France | |
| CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires | Nice | France | |
| AP-HP Hopital Pitie-Salpetriere | Paris | France | |
| Klinikum der Ludwig-Maximilians-Universitaet Muenchen | Munich | Germany | |
| Hadassah University Hospital | Jerusalem | Israel | |
| Fondazione IRCCS Ca'Granda Ospedale Maggiore | Milan | Italy | |
| Azienda Ospedale - Università Padova | Padova | Italy | |
| Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore | Rome | Italy | |
| Leids Universitair Medisch Centrum | Leiden | Netherlands | |
| Optimal Clinical Trials | Auckland | New Zealand |
+ 8 more sites — see the full list on the official registry below.
This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.
View NCT06066580 on ClinicalTrials.gov ↗ ← All trials in the UK