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Starting soon Early Phase 1

GSL Synthetase Inhibitor Plus GM-CSF and/ or Immune Checkpoint Inhibitor in Previously Treated High-Risk Neuroblastoma.

NCT07090538 · tracked via the Priya Life Science China tracker
Phase
Early Phase 1
Started
2025-08-01
Last updated
2025-07-29

Condition(s) studied

Neuroblastoma

Investigational drug(s) / intervention(s)

Eliglustat →

Eliglustat: Drug: GM-CSF + Eliglustat Granulocyte-Macrophage Colony Stimulating Factor (GM-CSF) and GSL Synthetase Inhibitor

Study summary

This exploratory clinical study will evaluate the efficacy and feasibility of combining a GSL synthase inhibitor with a granulocyte-macrophage colony stimulating factor (GM-CSF) in patients with advanced or metastatic neuroblastoma. Six to eight eligible patients are expected to be treated in this clinical trial: 1) Assessing the anti-tumour effects of GSL synthase inhibitors in combination with immune checkpoint inhibitors and/or GM-CSF; 2) To assess immunological or clinical predictive biomarkers of efficacy and toxicity; and 3) Detecting changes in the tumour microenvironment (TME) and the dynamics of peripheral blood immune cells after treatment with a GSL synthase inhibitor combined with GM-CSF.

Eligibility

Sex
ALL
Min age
6 Years
Max age
12 Years
Healthy volunteers
No
Inclusion Criteria: 1. Neuroblastoma must be documented at the point of diagnosis, which is defined as one of the following: histopathology of a biopsy of a solid tumour; bone marrow aspirate or biopsy suggestive of neuroblastoma with elevated blood or urine catecholamine metabolite levels. 2. The participant is at least 6years old at time of enrollment. 3. At least one measurable lesion at baseline according to RECIST version 1.1. 4. Have adequate organ function as assessed by the laboratory required by protocol, which should be confirmed within 2 weeks prior to the first dose of study drugs. 5. Previous treatment must be completed for more than 4 weeks prior to the enrollment of this study, and subjects have recovered to \<= grade 1 toxicity. 6. Eastern Cooperative Oncology Group (ECOG) performance status score≤2 and Estimated life expectancy of more than 3 months. 7. Patient(and/ or their parent/ legal guardian) is willing to participate and able to provide signed informed consent. Exclusion Criteria: 1. Any systemic anti-cancer therapy, including chemotherapy or immunotherapy, within 3 weeks before 1st dose of GM-CSF 2. Existing major organ dysfunction \> Grade 2, with the exception of hearing loss, hematological status, kidney and liver function 3. Active life-threatening infection 4. History of allergy or intolerance to study drug components. 5. The participant is CYP2D6 ultra-rapid metabolizer. 6. The participant is known to be allergy to Eliglustat. 7. The participant use drugs that will strongly inhibit CYP2D6 or CYP3A activity.

Primary outcome measure(s)

  • Objective response rate (ORR) — Up to 120 days after the last dose of study drugs
    Objective response rate includes complete response and partial response defined by investigators according to RECIST 1.1or iRECIST criteria.

Trial sites (2)

FacilityCityRegionStatus
Biotherapeutic Department and Hematology Department of Chinese PLA General Hospital Beijing China
Department of Pediatrics, The First Medical Center, Chinese PLA General Hospital Beijing China
Official registry record

This page summarises publicly available registry data for informational purposes — not medical advice. Eligibility is determined by each study team; patients should discuss participation with their clinician.

View NCT07090538 on ClinicalTrials.gov ↗ ← All trials in China